Update on Gene Therapy Trial for IQSEC2 Disease

November 5, 2025 Dear IQSEC2 family Update on new developments in the first clinical trial for IQSEC2 in boys with knockoutmutations and a second trial we are now planning for girls and also in the remainingboys with class 2 mutations (not knockout). Clinical trial in boys with knockout mutations.Pleased to report on a very productive…